Team
We are a team of experts in molecular biology, regulatory management, and clinical development
Sumathi Sivapalasingam, M.D.
Vice President, Head of Translational Medicine
Team

Panos Argiras
Senior Director, External Manufacturing

Helen Zhao, Ph.D.
Senior Director, Project Management

Elvin Ruan
Senior Director, Genome Editing

Salvatore Amato
Senior Director, Finance

Yasmin Khan
Senior Director, Project Management

Meriza Viray
Director, Clinical Operations

Ryo Takeuchi
Director, Genome Editing

Qin Xiang
Director, Analytical Development and QC

Adam Dunko
Director, Quality Assurance

Lucas Buchheim-Jurisson
Associate Director, Corporate Strategy

Meltem Isik
Associate Director, Bioinformatics

Shari Fox
Senior Clinical Trial Manager

Wenwen Huo
Senior Computational Biologist

Nadia Amrani, Ph.D.
Associate Director, Genome Editing

Xingting Yao
Data Scientist, Bioinformatics

Kevin Luk, Ph.D.
Scientist, Genome Editing
R&D Partners

Kamel Khalili, Ph.D.
Chief Scientific Founder
Temple University,
School of Medicine

Tricia Burdo, Ph.D.
Preclinical R&D
Temple University,
School of Medicine

Alexandra Howell, Ph.D.
Research Investigator
Veterans Affairs Medical Center & Geisel School of Medicine at Dartmouth

Sujeewa Lellupitiyage Don, Ph.D.
Scientist, Genome Editing

Raquel Duran
Talent & Workplace Operations Specialist

Karina Dias Teixeira
Sr. Scientist, Molecular Biology

Pamela Castillo
Senior Corporate Development Associate

Wolfgang Weiss
Intern, Program and Portfolio Management
Sam Slattery
Senior Scientist, Nonviral Delivery


Ilker Sariyer, DVM Ph.D.
Research Investigator
Temple University,
School of Medicine

Matt Hayden, M.D. Ph.D.
Research Investigator
Dartmouth-Hitchcock Medical Center

Amir Khalili, M.S.
Program Manager
Temple University, School of Medicine

Niles Donegan, Ph.D.
Principal Scientist
Previous: Geisel School of Medicine at Dartmouth
Scientific Advisory Board
John Baxter, M.D.
Cooper University Medical Center
(HIV Clinician)
Toni Cathomen, Ph.D.
Albert-Ludwigs-Universitat Freiburg
(Gene Therapy)
Joseph Berger, M.D.
Perelman School of MedicineUniversity of Pennsylvania
(JC Virus & PML)
Nicole Paulk, Ph.D.
University of California San Francisco
(Oncology & AAV)
Lisa Danzig, M.D.
Life Sciences Executive
(Global Health)
David Thomas, M.D.
Johns Hopkins School of Medicine
(Hepatitis B)
David Clifford, M.D.
Washington University School of Medicine in St. Louis
(PML and HIV)
Joseph Bondy-Denomy, Ph.D.
University of California San Francisco
(CRISPR Inhibitors)
Keith Jerome, M.D., Ph.D.
Fred Hutchinson Cancer
Research Center
(Herpes Simplex Viruses, Hepatitis B)
Kamel Khalili, PhD
Temple University School of Medicine (Neurovirology and Gene Therapy)
Mike Walker, Ph.D.
Stanford University
(Bioinformatics)
Kenneth L. Tyler, M.D.University of Colorado Denver – Anschutz Medical Campus(JC Virus & PML)
Timothy M. Block, Ph.D.
Baruch S. Blumberg Institute
(Hepatitis B)